Safety and Preliminary Efficacy of VG801 in Patients With ABCA4 Mutation-associated Retinal Dystrophy (Stargardt Disease)
Abroad (travel likely)RecruitingPHASE1, PHASE2
Conditions
Retinal Dystrophy Due to Biallelic ABCA4 Mutations · Stargardt Disease 1
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Shanghai General Hospital, Shanghai, Shanghai Municipality, China
Contact: Principal Investigator (Xiaodong Sun, MD)
Study leads
Xiaodong Sun, MD
Principal Investigator
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine