Gene Therapy for Alpha 1- Antitrypsin Deficiency

Abroad (travel likely)RecruitingPHASE1

Conditions

Alpha 1-Antitrypsin Deficiency

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations

WCMC Department of Genetic Medicine, New York, New York, United States
Contact: Study coordinator (Sandra Hyde) · sah2003@med.cornell.edu · 646-962-2672
Contact: Study coordinator (Niamh Savage) · nis2049@med.cornell.edu · 646-962-5527
Contact: Principal Investigator (Ronald Crystal, MD)

Study leads

Ronald G Crystal, MD
Principal Investigator
Weill Medical College of Cornell University

View source on ClinicalTrials.gov

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