Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients
Conditions
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Cancer Institute of New Jersey, New Brunswick, New Jersey, United States
Contact: Principal Investigator (Richard DRACHTMAN)Childrens Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Contact: Principal Investigator (Timothy Olson)St Jude Childrens Research Hospital, Memphis, Tennessee, United States
Contact: Principal Investigator (Marcin Wlodarski)Novartis Investigative Site, Brasília, Federal District, Brazil
Novartis Investigative Site, Natal, Rio Grande do Norte, Brazil
Novartis Investigative Site, Porto Alegre, Rio Grande do Sul, Brazil
Novartis Investigative Site, Santo André, São Paulo, Brazil
Novartis Investigative Site, São Paulo, São Paulo, Brazil
Novartis Investigative Site, São Paulo, São Paulo, Brazil
Novartis Investigative Site, Cali, Valle del Cauca Department, Colombia
Novartis Investigative Site, Berlin, Germany
Novartis Investigative Site, Genova, GE, Italy
Novartis Investigative Site, Utrecht, Netherlands
Study leads
Novartis Pharmaceuticals
Study Director
Novartis Pharmaceuticals