Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)
Conditions
Leber Congenital Amaurosis 10 · Blindness · Leber Congenital Amaurosis · Sensation Disorders · Vision Disorder · Neurological Manifestations · Eye Diseases, Hereditary · Eye Diseases · Eye Disorders Congenital · Retinal Disease
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This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
UCSF Wayne and Gladys Valley Center for Vision, San Francisco, California, United States
University of Miami - Bascom Palmer Eye Institute, Miami, Florida, United States
University of Iowa, Iowa City, Iowa, United States
University of Minnesota Medical School, Minneapolis, Minnesota, United States
University of Pennsylvania - Center for Advanced Retinal & Ocular Therapeutics, Philadelphia, Pennsylvania, United States
Universitair Ziekenhuis Gent (UZ), Ghent, Belgium
INRET Clínica/ Santa Casa de Misericórdia de Belo Horizonte, Belo Horizonte, Minas Gerais, Brazil
Federal University of São Paulo - Hospital São Paulo (UNIFESP-HSP), São Paulo, São Paulo, Brazil
University of Alberta, Edmonton, Alberta, Canada
The Hospital for Sick Children - SickKids, Toronto, Ontario, Canada
Centre de maladies rares CHNO des Quinze Vingt, Paris, France
Justus-Liebig Universität - Department of Ophthalmology, Giessen, Germany
Klinikum der Ludwig-Maximilian Universität München, München, Germany
University of Tuebingen - Inst. for Ophthalmic Research, Tübingen, Germany
Radboud Universitair Medisch Centrum, Nijmegen, Netherlands
Hospital Sant Joan de Déu (SJD Barcelona Children's Hospital), Barcelona, Spain
Moorfields Eye Hospital NHS Foundation Trust, London, United Kingdom