A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
מצבים רפואיים
Myotonic Dystrophy
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
University of Florida, 2004 Mowry Road - Site Number: 8400005, Gainesville, Florida, United States
Contact: Principal Investigator (Dr. Subramony)University of South Florida - Neuromuscular Research, 13330 USF Laurel Drive - Site Number: 8400001, Tampa, Florida, United States
Contact: Principal Investigator (Dr. Tuan Vu)Columbia University Medical Center - Neurological Institute, 710 W. 168th, 2nd floor, suite 204 - Site Number : 8400003, New York, New York, United States
Contact: Principal Investigator (Dr. Christina Ulane)Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond, Virginia, United States
Hospital Italiano de Buenos Aires, Juan Domingo Peron 4190 - Site Number: 0320001, Buenos Aires, Argentina
Contact: Study coordinator (Ventura Simonovich) · ventura.simonovich@hospitalitaliano.org.ar · 54 11 4959 0200Contact: Principal Investigator (Ventura Simonovich)Investigational Site Number : 0360001, Brisbane, Queensland, Australia
The Montreal Neurological Institute and Hospital, 3801 rue University - Site Number: 1240001, Montreal, Quebec, Canada
Contact: Principal Investigator (Dr. Erin O'Ferrall)Investigational Site Number : 3760002, Ramat Gan, Israel
Investigational Site Number : 8260002, Newcastle upon Tyne, United Kingdom