A Phase 3 Study of NTLA-2001 in ATTRv-PN
Conditions
Neuromuscular Disease · Neuromuscular Diseases (NMD) · Neurodegenerative Disease · Neurodegenerative Disease, Hereditary · Neurodegenerative Diseases · Neuromuscular Diseases · Nerve Disorders · Nervous System Disease · Nervous System Diseases · Genetic Disease, Inborn · Amyloidosis, Familial · Amyloidosis, Hereditary · Amyloidosis · Polyneuropathies · Amyloid Neuropathies · Amyloid Neuropathies, Familial · Peripheral Nervous System Disease · Peripheral Nervous System Diseases · Metabolism, Inborn Errors · Metabolic Diseases
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Hospital Británico de Buenos Aires, Buenos Aires, Argentina
Hospital Italiano de Buenos Aires (HIBA), Buenos Aires, Argentina
Hospital El Cruce, San Juan Bautista, Argentina
Hospital das Clinicas da Universidade Estadual de Campinas (UNICAMP), Campinas, Brazil
HCFMRP - Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto, Ribeirão Preto, Brazil
Instituto de Educacao, Pesquisa e Gestao em Saude, Rio de Janeiro, Brazil
PSEG Centro de Pesquisa Clinica S.A., São Paulo, Brazil
National Institute of Medical Sciences and Nutrition - Salvador Zubiran (INCMNSZ), Tlalpan, Mexico
National University Hospital, Singapore, Singapore
Singapore General Hospital, Singapore, Singapore
National Taiwan University Hospital, Taipei, Taiwan
Taipei Veterans General Hospital, Taipei, Taiwan
Chang Gung Medical Foundation - Linkou Branch, Taoyuan, Taiwan
Siriraj Hospital, Bangkok, Thailand