A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B
Conditions
Hemophilia B
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Orthopaedic Hemophilia Treatment Center, Los Angeles, California, United States
David Geffen School of Medicine at UCLA, Los Angeles, California, United States
Children's Hospital Los Angeles, Los Angeles, California, United States
University of California Davis, Sacramento, California, United States
University California San Francisco, San Francisco, California, United States
University of Colorado Hemophilia and Thrombosis Center, Aurora, Colorado, United States
Yale HTC, New Haven, Connecticut, United States
University of Florida, Gainesville, Florida, United States
Indiana Hemophilia and Thrombosis Center, Indianapolis, Indiana, United States
Tulane University School of Medicine, Louisiana Center for Bleeding and Clotting Disorders, New Orleans, Louisiana, United States
University of Michigan, Ann Arbor, Michigan, United States
Nationwide Children's Hospital, Columbus, Ohio, United States
Children's Hospital of Philadelphia (CHOP), Philadelphia, Pennsylvania, United States
Vanderbilt University Medical Center, Nashville, Tennessee, United States
Royal Prince Alfred Hospital, Haemophilia Treatment Centre, Camperdown, New South Wales, Australia
Royal Brisbane and Women's Hospital, Herston, Queensland, Australia
Royal Adelaide Hospital, Adelaide, South Australia, Australia
University of Alberta Hospital, Edmonton, Alberta, Canada
McMaster University Medical Centre - Hamilton Health Sciences, Hamilton, Ontario, Canada
McGill University Health Center (MUHC), Montreal, Quebec, Canada
Hospices Civils de Lyon, Bron, Lyon, France
Hemostase Clinique, Institut Coeur Poumon, Lille, Nord, France
Hopital Necker, Paris, Île-de-France Region, France
University Hospital Frankfurt, Frankfurt am Main, Hesse, Germany
University Hospital Hamburg Eppendorf, Hamburg, Germany
Careggi University Hospital, Florence, Firenze, Italy
Fondazione Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) Ca Granda Ospedale Maggiore Policlinico, Milan, Lombardy, Italy
Irccs Humanitas Research Hospital, Rozzano, Lombardy, Italy
Ospedale san Bortolo, Vicenza, Italy
Hospital Universitario Virgen del Rocio, Seville, Andalusia, Spain
Complejo Hospitalario Universitario de A Coruña (Edificio Teresa Herrera-Materno Infantil), A Coruña, Galicia, Spain
Hospital Clinico Universitario Virgen De La Arrixaca, El Palmar, Murcia, Spain
Hospital Universitario Central de Asturias, Oviedo, Principality of Asturias, Spain
Hospital Universitario Vall d'Hebron, Barcelona, Spain
Hospital Universitario La Paz, Madrid, Spain
Haemostasis and Thrombosis Unit, Hospital La Fe, Valencia, Spain
Hospital Universitario Miguel Servet, Zaragoza, Spain
Glasgow Royal Infirmary - Clinical Research Facility, Glasgow, Scotland, United Kingdom
Queen Elizabeth Hospital Birmingham, Birmingham, West Midlands, United Kingdom
Addenbrooke's Hospital, Cambridge University Hospitals NHS FT, Cambridge, United Kingdom
Pathology and Pharmacy Building, The Royal London Hospital, London, United Kingdom
Royal Free London NHS Foundation Trust, London, United Kingdom
St. Thomas' Hospital, London, United Kingdom
Hammersmith Hospital Comprehensive Care Centre, London, United Kingdom
Study leads
Clinical Trial Management
Study Director
Regeneron Pharmaceuticals