ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia

Abroad (travel likely)RecruitingPHASE1, PHASE2

Conditions

Beta-Thalassemia

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations

Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Contact: Study coordinator (Janet Kwiatkowski, MD) · kwiatkowski@chop.edu · 215-590-5286
Contact: Study coordinator (Jaladhikumar Patel) · patelj23@chop.edu · 267-426-5602
Contact: Principal Investigator (Janet Kwiatkowski, MD)

Study leads

Janet Kwiatkowski, MD
Principal Investigator
Children's Hospital of Philadelphia

View source on ClinicalTrials.gov

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