First in Human (FIH) Study of ALN-SOD in Adult Participants With Amyotrophic Lateral Sclerosis Associated With Mutation in the SOD1 Gene (SOD1-ALS)
Conditions
Amyotrophic Lateral Sclerosis (ALS) · Mutation in the Superoxide Dismutase-1 (SOD1) Gene
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Concord Repatriation General Hospital, Concord, New South Wales, Australia
Macquarie University, Sydney, New South Wales, Australia
Sunshine Coast University Hospital, Birtinya, Queensland, Australia
KU Leuven, Leuven, Vlaams-Brabant, Belgium
University of Alberta Hospital, Edmonton, Division of Neurology, Edmonton, Alberta, Canada
University Hospital - London Health Sciences Centre, London, Ontario, Canada
Sunnybrook Research Institute, Toronto, Ontario, Canada
Montreal Neurological Institute and Hospital, Montreal, Quebec, Canada
Hokkaido University Hospital, Sapporo, Hokkaido, Japan
Tokushima University Hospital, Tokushima, Tokushima, Japan
Toho University Omori Medical Center, Ōta-ku, Tokyo, Japan
Kyoto University Hospital, Kyoto, Japan
Hanyang University Seoul Hospital, Seoul, South Korea
Seoul National University Hospital, Seoul, South Korea
Noorlands University Hospital-Department of Neurology, Umeå, Noorland, Sweden
Kaohsiung Chang Gung Memorial Hospital, Kaohsiung City, Taiwan
Taipei Veterans General Hospital, Taipei, Taiwan
Study leads
Clinical Trial Management
Study Director
Regeneron Pharmaceuticals