Study of ATX-01 in Participants With DM1

Abroad (travel likely)RecruitingPHASE1, PHASE2

Conditions

Myotonic Dystrophy 1

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • UCLA, Los Angeles, California, United States

    Contact: Study coordinator (Michael Yan) · MYan@mednet.ucla.edu · 310-825-3264
    Contact: Principal Investigator (Perry Shieh, MD, PhD)
  • University of Florida, Gainesville, Florida, United States

    Contact: Study coordinator (Brandy Donahue-Quails) · Brandy.Donahue-Quails@neurology.ufl.edu
  • University of Iowa Health Care - Department of Neurology, Iowa City, Iowa, United States

    Contact: Study coordinator (Heena Olalde) · heena-olalde@uiowa.edu · 319-356-8326
    Contact: Principal Investigator (Andrea Swenson)
  • University of Kansas Medical Center, Department of Neurology, Fairway, Kansas, United States

    Contact: Study coordinator (Cassidy Nelson) · cnelson15@kumc.edu · 913-588-3653
  • Virginia Commonwealth University, Richmond, Virginia, United States

    Contact: Study coordinator (Jodie Howell) · jodie.howell@vcuhealth.org · 804-828-6110
    Contact: Principal Investigator (Nicholas Johnson, MD)
  • Centre Intégré Universitaire de Santé et Services Sociaux du Saguenay-Lac-St-Jean, Chicoutimi, Quebec, Canada

    Contact: Study coordinator (Sabrina Côté) · sabrina.cote.inf@ssss.gouv.qc.ca · 418-541-1000
  • Institute of Myology, Paris, France

    Contact: Study coordinator (Study Co-ordinator) · essais-adultes@institut-myologie.org
  • The NeMO Clinical Center in Milan, Neurorehabilitation Unit, University of Milan, Milan, Italy

    Contact: Study coordinator (Clinical Research Co-ordinator) · crc_rsu@centrocliniconemo.it
  • Fondazione Policlinico A. Gemelli- IRCCS, Rome, Italy

  • Radboudumc, Nijmegen, Netherlands

    Contact: Study coordinator (Spierziekten Research Team Radboudumc) · spierziektenresearchteam@radboudumc.nl
    Contact: Principal Investigator (K Mul)
  • Hospital Universitario Donostia, Donostia / San Sebastian, Spain

    Contact: Study coordinator (Ioana Croitoru) · IOANA.CROITORU@bio-gipuzkoa.eus
    Contact: Principal Investigator (Adolfo López de Munain Arregui)
  • St. George's University Hospital, London, United Kingdom

    Contact: Study coordinator (Joana Teixeira) · Joana.Teixeira@stgeorges.nhs.uk
    Contact: Principal Investigator (Emma Matthews)