A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel
Conditions
Beta-Thalassemia
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
UCSF Benioff Children's Hospitals, Oakland, California, United States
Stanford University, Palo Alto, California, United States
University of Minnesota, Minneapolis, Minnesota, United States
Cohen Children's Medical Center, New Hyde Park, New York, United States
Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Texas Children's Hospital, Houston, Texas, United States
Study leads
Himal Lal Thakar, MD
Study Director
bluebird bio, Inc.