Gene Therapy Trial for Otoferlin Gene-mediated Hearing Loss
Conditions
Sensorineural Hearing Loss, Bilateral
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
University of California, San Francisco Benioff Children's Hospital, San Francisco, California, United States
University of Iowa, Iowa City, Iowa, United States
Boston Children's Hospital, Boston, Massachusetts, United States
Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Vanderbilt Bill Wilkerson Center, Nashville, Tennessee, United States
The Hospital for Sick Children Jaina.negandhi@sickkids.ca +1 (416) 813 6683, Toronto, Ontario, Canada
National Taiwan University Hospital, Taipei, Taiwan
University College London, London, United Kingdom, United Kingdom
Study leads
Peter Marks, MD
Study Director
Eli Lilly and Company