A Study of DB-OTO, an Adeno-Associated Virus (AAV) Based Gene Therapy, in Children/Infants, Adolescents and Adults With Hearing Loss Due to Otoferlin Mutations

חו"ל (דורש נסיעה)מגייס משתתפיםPHASE1, PHASE2

מצבים רפואיים

Congenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)

סיכום בשפה פשוטהבעזרת בינה מלאכותית

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים
  • University of California Los Angeles Medical Center, Los Angeles, California, United States

    Contact: Study coordinator (Akira Ishiyama) · ishiyama@g.ucla.edu
  • Rady Children's Hospital, San Diego, California, United States

    Contact: Study coordinator (Daniela Carvalho) · dcarvalho@rchsd.org
  • Nemours Children s Clinic, Jacksonville, Florida, United States

    Contact: Study coordinator (Evie Landry) · evie.Landry@nemours.org
  • Nemours Childrens Hospital, Orlando, Florida, United States

    Contact: Study coordinator (Cedric Pritchett) · cedric.Pritchett@nemours.org
  • Boston Children's Hospital - Main, Boston, Massachusetts, United States

    Contact: Study coordinator (Eliot Shearer) · Eliot.Shearer@childrens.harvard.edu
  • Columbia University Irving Medical Center, New York, New York, United States

    Contact: Study coordinator (Lawrence Lustig) · lustig@columbia.edu
  • Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States

    Contact: Study coordinator (John Greinwald, Jr.) · john.greinwald@cchmc.edu
  • Seattle Children's Hospital, Seattle, Washington, United States

    Contact: Study coordinator (Jay Rubenstein) · rubinj@uw.edu
  • Medical College of Wisconsin, Milwaukee, Wisconsin, United States

    Contact: Study coordinator (Sarah Mleziva) · smleziva@mcw.edu
  • University Hospital Tubingen, Tübingen, Germany

    Contact: Study coordinator (Hubert Lowenheim) · hubert.loewenheim@uni-tuebingen.de
  • Shinshu University Hospital, Matsumoto-shi, Nagano, Japan

    Contact: Study coordinator (Yutaka Takumi) · takumi@shinshu-u.ac.jp
  • Clinica Universidad de Navarra- Pamplona, Pamplona, Navarre, Spain

    Contact: Study coordinator (Manuel Jesus Manrique Rodriguez) · mmanrique@unav.es
  • Hospital Universitario Materno Infantil en las Palmas de Gran Canaria, Las Palmas de Gran Canaria, Spain

  • Ramon y Cajal University Hospital, Madrid, Spain

    Contact: Study coordinator (Ruben Polo) · rubenpolo1979@gmail.com
  • Addenbrooke's Hospital, Cambridge University Hospitals NHS FT, Cambridge, United Kingdom

    Contact: Study coordinator (Manohar Bance) · mlb59@cam.ac.uk
  • Great Ormond Street Hospital For Children NHS Foundation Trust, London, United Kingdom

    Contact: Study coordinator (Robert Nash) · r.nash@ucl.ac.uk
מובילי המחקר
  • Clinical Trial Management

    Study Director

    Regeneron Pharmaceuticals