A Study of DB-OTO, an Adeno-Associated Virus (AAV) Based Gene Therapy, in Children/Infants, Adolescents and Adults With Hearing Loss Due to Otoferlin Mutations
מצבים רפואיים
Congenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
University of California Los Angeles Medical Center, Los Angeles, California, United States
Rady Children's Hospital, San Diego, California, United States
Nemours Children s Clinic, Jacksonville, Florida, United States
Nemours Childrens Hospital, Orlando, Florida, United States
Boston Children's Hospital - Main, Boston, Massachusetts, United States
Columbia University Irving Medical Center, New York, New York, United States
Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
Seattle Children's Hospital, Seattle, Washington, United States
Medical College of Wisconsin, Milwaukee, Wisconsin, United States
University Hospital Tubingen, Tübingen, Germany
Shinshu University Hospital, Matsumoto-shi, Nagano, Japan
Clinica Universidad de Navarra- Pamplona, Pamplona, Navarre, Spain
Hospital Universitario Materno Infantil en las Palmas de Gran Canaria, Las Palmas de Gran Canaria, Spain
Ramon y Cajal University Hospital, Madrid, Spain
Addenbrooke's Hospital, Cambridge University Hospitals NHS FT, Cambridge, United Kingdom
Great Ormond Street Hospital For Children NHS Foundation Trust, London, United Kingdom
מובילי המחקר
Clinical Trial Management
Study Director
Regeneron Pharmaceuticals