An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.
Abroad (travel likely)RecruitingEARLY_PHASE1
Conditions
Aromatic L-amino Acid Decarboxylase (AADC) Deficiency
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Shanghai Children's Medical Center Affiliated to Shanghai Jiao Tong University School of Medicine, Shanghai, No. 1678, Dongfang Road, Pudong New Area, Shanghai, China
Study leads
Jiwen Wang, Doctor
Study Chair
Shanghai Children's Medical Center, affiliated to Shanghai Jiao Tong University School of Medicine