A Clinical Trial of PRAX-222 in Pediatric Participants With Early Onset SCN2A Developmental and Epileptic Encephalopathy

Abroad (travel likely)RecruitingPHASE1, PHASE2

Conditions

SCN2A-DEE · Epilepsy

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Le Bonheur Childrens Hospital, Memphis, Tennessee, United States

  • Hospital de Clinicas de Porto Alegre, Porto Alegre, Rio Grande do Sul, Brazil

    Contact: Study coordinator (Bruna de Souza, Research Coordinator) · bpinheiro@hcpa.edu.br · +55 513-359-6343
    Contact: Study coordinator (Larissa Pozzebon da Silva, Research Coordinator)
    Contact: Principal Investigator (Roberto Giugliani)
  • Praxis Research Site, São Paulo, Brazil

    Contact: Study coordinator (Alessandra Vieira) · alevrodrigues@gmail.com
    Contact: Principal Investigator (Kette Valente, MD)
Study leads
  • Medical Director

    Study Director

    Praxis Precision Medicines