Study to Check the Safety of Fazirsiran and Learn if Fazirsiran Can Help People With Liver Disease and Scarring (Fibrosis) Due to an Abnormal Version of Alpha-1 Antitrypsin Protein
מצבים רפואיים
Alpha1-Antitrypsin Deficiency
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
University of Alabama at Birmingham, Birmingham, Alabama, United States
Contact: Principal Investigator (Meagan Gray)St. Joseph's Hospital and Medical Center, Phoenix, Arizona, United States
Contact: Principal Investigator (Nilofar Najafian)Mayo Clinic, Phoenix, Arizona, United States
Contact: Principal Investigator (Hugo Vargas)University of Arizona Thomas D. Boyer Liver Institute, Tucson, Arizona, United States
Gastroenterology & Liver Institute, Escondido, California, United States
University of California San Diego, Altman Clinical and Translational Institute, La Jolla, California, United States
Contact: Principal Investigator (Rohit Loomba)UCLA Pulmonary and Critical Care, Los Angeles, California, United States
Contact: Principal Investigator (Igor Barjaktarevic)Stanford University, Palo Alto, California, United States
Contact: Principal Investigator (Paul Kwo)University of California Benioff Children's Hospital, San Francisco, California, United States
Contact: Principal Investigator (Philip Rosenthal)Peak Gastroenterology Associates, PC, Colorado Springs, Colorado, United States
Contact: Principal Investigator (Bhaktasharan Patel)University of Florida, Gainesville, Florida, United States
Contact: Principal Investigator (Virginia Clark)Schiff Center for Liver Diseases/University of Miami, Miami, Florida, United States
Contact: Principal Investigator (Eugene Schiff)Children's Healthcare of Atlanta, Atlanta, Georgia, United States
Indiana University School of Medicine - Indianapolis, Indianapolis, Indiana, United States
Contact: Principal Investigator (Raj Vuppalanchi)University of Iowa Hospitals and Clinics, Iowa City, Iowa, United States
Contact: Principal Investigator (Tomohiro Tanaka)Ochsner Medical Center, New Orleans, Louisiana, United States
Contact: Principal Investigator (George Therapondos)University of Maryland Medical Center, Baltimore, Maryland, United States
Contact: Principal Investigator (Kirti Shetty)Brigham and Womens Hospital, Boston, Massachusetts, United States
Contact: Principal Investigator (Nikroo Hashemi)Boston Medical Center, Boston, Massachusetts, United States
Contact: Principal Investigator (Arpan Mohanty)University of Michigan Hospital, Ann Arbor, Michigan, United States
Contact: Principal Investigator (Robert Fontana)Henry Ford Medical Center - Columbus, Novi, Michigan, United States
Contact: Principal Investigator (Stuart Gordon)Mayo Clinic - PPDS, Rochester, Minnesota, United States
Contact: Principal Investigator (Harmeet Malhi)Cardinal Glennon Children's Hospital, St Louis, Missouri, United States
Contact: Principal Investigator (Jeffery Teckman)Washington University School of Medicine in St. Louis, St Louis, Missouri, United States
Contact: Principal Investigator (Scott McHenry)NYU Langone Health, New York, New York, United States
Contact: Principal Investigator (Viviana Figueroa Diaz)Morgan Stanley Childrens Hospital of New York Presbyterian (CHONY) - PIN, New York, New York, United States
Columbia University Irving Medical Center, New York, New York, United States
Contact: Principal Investigator (Monica Goldklang)University Hospitals Cleveland Medical Center, Cleveland, Ohio, United States
Contact: Principal Investigator (Seth Sclair)Penn State Health Milton S. Hershey Medical Center, Hershey, Pennsylvania, United States
Contact: Principal Investigator (Timothy Craig)Temple University Hospital, Philadelphia, Pennsylvania, United States
Contact: Principal Investigator (Yedidya Saiman)Medical University of South Carolina, Charleston, South Carolina, United States
Contact: Principal Investigator (Charlie Strange)Vanderbilt University Medical Center, Nashville, Tennessee, United States
Contact: Principal Investigator (Roman Perri)Texoma Liver Center, Denison, Texas, United States
Contact: Principal Investigator (Hesham Elgouhari)Baylor College of Medicine Medical Center, Houston, Texas, United States
Contact: Principal Investigator (George Cholankeril)The Texas Liver Institute, San Antonio, Texas, United States
Contact: Principal Investigator (Eric Lawitz)Bon Secours St. Mary's Hospital, Richmond, Virginia, United States
Contact: Principal Investigator (Mitchell Shiffman)VCU Medical Center North Hospital, Richmond, Virginia, United States
Contact: Principal Investigator (Amon Asgharpour)Royal Adelaide Hospital, Adelaide, South Australia, Australia
St Vincents Hospital Melbourne - PPDS, Fitzroy, Victoria, Australia
Contact: Principal Investigator (Matthew Conron)LKH-Universitätsklinikum Graz, Graz, Austria
Contact: Principal Investigator (Martin Wagner)Medizinische Universität Innsbruck, Innsbruck, Austria
Contact: Study coordinator (Site Contact) · heinz.zoller@i-med.ac.at; hepa-studyteam@i-med.ac.at · +4351250482830Contact: Principal Investigator (Heinz Zoller)Klinikum Klagenfurt Am Wörthersee, Klagenfurt, Austria
Contact: Principal Investigator (Markus Peck-Radosavljevic)Medizinische Universität Wien (Medical University of Vienna), Vienna, Austria
Contact: Principal Investigator (Mattias Mandorfer)UZ Antwerpen, Antwerp, Belgium
Contact: Principal Investigator (Sven Francque)UZ Leuven, Leuven, Belgium
Contact: Principal Investigator (Jef Verbeek)Hospital de Base do Distrito Federal, Brasília, Brazil
Contact: Principal Investigator (Liliana Mendes Sampaio Costa)Hospital Sirio-Libanes, São Paulo, Brazil
Contact: Principal Investigator (Gilda Porta)Universidade Estadual Paulista Julio de Mesquita Filho Faculdade de Medicina Campus de Botucatu, São Paulo, Brazil
Contact: Principal Investigator (Fernando Romeiro Gomes)GI Research Institute, Vancouver, British Columbia, Canada
Contact: Principal Investigator (Hin Hin Ko)Queen Elizabeth II Health Sciences Center, Halifax, Nova Scotia, Canada
Contact: Principal Investigator (Julie Zhu)Inspiration Research Limited, Toronto, Ontario, Canada
Contact: Principal Investigator (Kenneth Chapman)Institut klinicke a experimentalni mediciny, Prague, Czechia
Contact: Principal Investigator (Jan Sperl)Hvidovre Hospital, Hvidovre, Denmark
Contact: Principal Investigator (Elias Rashu)Hôpital Beaujon, Clichy, France
Contact: Principal Investigator (Kathleen Milord)Hôpital de La Croix Rousse, Lyon, France
Contact: Principal Investigator (Teresa Antonini)Centre Francois Magendie, Pessac, France
Contact: Principal Investigator (Maeva Zysman)Hopital PONTCHAILLOU CHU de Rennes, Rennes, France
Contact: Principal Investigator (Edouard Bardou-Jacquet)Hospital Purpan, Toulouse, France
Contact: Principal Investigator (Lauren Alric)Hôpital Paul Brousse, Val-de-Marne, France
Contact: Principal Investigator (Audrey Coilly)Universitätsklinikum der RWTH Aachen, Aachen, Germany
Contact: Principal Investigator (Pavel Strnad)Charité - Campus Virchow-Klinikum-Ostring 1, Berlin, Germany
Contact: Principal Investigator (Frank Tacke)Hannover Medical School, Hanover, Germany
Contact: Principal Investigator (Heiner Wedemeyer)Universitätsklinikum Schleswig-Holstein - Campus Kiel, Kiel, Germany
Contact: Principal Investigator (Rainer Günther)Universitätsklinikum Tübingen, Tübingen, Germany
Contact: Principal Investigator (Christoph Berg)Beaumont Hospital, Dublin, Ireland
Contact: Principal Investigator (Noel McElvaney)Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milan, Italy
Contact: Principal Investigator (Luca Valenti)Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone, Palermo, Italy
Contact: Principal Investigator (Vincenza Calvaruso)Fondazione IRCCS Policlinico San Matteo di Pavia, Pavia, Italy
Contact: Principal Investigator (Angelo Corsico)IRCCS Istituto Clinico Humanitas, Rozzano, Italy
Contact: Principal Investigator (Alessio Aghemo)Amsterdam UMC - VUmc - De Boelelaan, Amsterdam, Netherlands
Leiden University Medical Center, Leiden, Netherlands
Contact: Principal Investigator (Emily F.A. van 't Wout)ID Clinic Arkadiusz Pisula, Śląskie, Poland
WIP Warsaw IBD Point Profesor Kierkus, Warsaw, Poland
Contact: Principal Investigator (Jaroslaw Kierkus)CCA Hospital Braga, Braga, Portugal
Contact: Principal Investigator (Carla Rolanda)Hospital Nélio Mendonça, Funchal, Portugal
Contact: Principal Investigator (Vitor Pereira)Centro Hospitalar do Porto, Porto, Portugal
Contact: Principal Investigator (Luis Maia)Hospital Universitario Vall d'Hebron - PPDS, Barcelona, Spain
Contact: Principal Investigator (Monica Pons Delgado)Hospital Universitario Virgen de la Victoria, Málaga, Spain
Contact: Principal Investigator (Raul Andrade)Hospital Universitario Marques de Valdecilla, Santander, Spain
Contact: Principal Investigator (Alvaro Gonzalez)Hospital Universitario Virgen del Rocio - PPDS, Seville, Spain
Contact: Principal Investigator (Manuel Romero Gómez)Karolinska Universitetssjukhuset Huddinge, Huddinge, Sweden
Contact: Principal Investigator (Staffan Wahlin)Universitetssjukhuset i Linköping, Linköping, Sweden
Contact: Principal Investigator (Mattias Ekstedt)Inselspital Bern, Bern, Switzerland
Contact: Principal Investigator (Guido Stirnimann)Addenbrooke's Hospital, Cambridge, United Kingdom
Contact: Principal Investigator (Willliam Griffiths)Royal Infirmary of Edinburgh, Edinburgh, United Kingdom
Contact: Principal Investigator (Michael Williams)Royal Free Hospital, London, United Kingdom
Contact: Principal Investigator (Aileen Marshall)King's College Hospital, London, United Kingdom
Contact: Principal Investigator (Aftab Ala)Queen's Medical Centre, Nottingham, United Kingdom
Derriford Hospital, Plymouth, United Kingdom
Contact: Principal Investigator (Ashwin Dhanda)
מובילי המחקר
Study Director
Takeda