Melpida: Recombinant Adeno-associated Virus (Serotype 9) Encoding a Codon Optimized Human AP4M1 Transgene (hAP4M1opt)
Abroad (travel likely)RecruitingPHASE1, PHASE2
Conditions
Spasticity, Muscle · Microcephaly · Intellectual Deficiency · Growth Retardation · SPG50 · Spastic Paraplegia
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Children's Medical Center Dallas, Dallas, Texas, United States
Contact: Study coordinator (SUSAN IANNACCONE, MD) · SUSAN.IANNACCONE@UTSouthwestern.edu · 214/456-5220
Study leads
Susan T. Iannaccone, MD, FAAN
Principal Investigator
University of Texas Southwestern Medical Center