A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome
מצבים רפואיים
Dravet Syndrome
סיכום בשפה פשוטהבעזרת בינה מלאכותית
הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.
מיקומים
UCSF Benioff Children's Hospitals, San Francisco, California, United States
Contact: Principal Investigator (Adam Numis)Colorado Children's Hospital, Aurora, Colorado, United States
Nicklaus Children's Hospital, Miami, Florida, United States
Contact: Study coordinator (Dainelys Pena Rodriguez) · Dainelys.PenaRodriguez@nicklaushealth.org · 786-624-3547Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
Contact: Principal Investigator (Linda Laux)Boston Children's Hospital, Boston, Massachusetts, United States
Mott Children's Hospital, Ann Arbor, Michigan, United States
Mayo Clinic, Rochester, Minnesota, United States
Duke Children's Hospital & Health Center, Durham, North Carolina, United States
Nationwide Children's Hospital, Columbus, Ohio, United States
Oregon Health and Science University (OSHU), Portland, Oregon, United States
Cook Children's Medical Center, Fort Worth, Texas, United States
Contact: Study coordinator (Dianna Grado, RN, CCRC) · Dianna.Grado@cookchildrens.org · (682) 885-2844Contact: Principal Investigator (Scott Perry)The Royal Children's Hospital, Melbourne, Australia
Contact: Study coordinator (Prof. Ingrid Scheffer)Contact: Study coordinator (Dr. Katherine Howell)Queen Elizabeth Hospital, Glasgow, United Kingdom
Great Ormond Street Hospital, London, United Kingdom
מובילי המחקר
Salvador Rico, M.D., Ph.D
Study Director
Encoded Therapeutics