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A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C

Abroad (travel likely)RecruitingPHASE3

Conditions

Niemann-Pick Disease, Type C

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations

  • Mayo Clinic, Rochester, Minnesota, United States

  • The Royal Melbourne Hospital, Parkville, Victoria, Australia

  • First Faculty of Medicine, Charles University Hospital Prague, Prague, Czechia

  • University of Giessen, Giessen, Germany

  • University of Hamburg, Hamburg, Germany

  • SphinCS - Institute of Clinical Science in Lysosomal Storage Disorders, Höchheim, Germany

  • Ludwig Maximilian University of Munich, München, Germany

    Contact: Study coordinator (Susanne Schneider-Pils, MD) · susanne.schneider@med.uni-muenchen.de · +49 (0)89 4400 7677
    Contact: Principal Investigator (Susanne Schneider-Pils, MD)

  • University Hospital Münster, Münster, Germany

  • Amsterdam UMC, Amsterdam, Netherlands

    Contact: Study coordinator (Marion Brands, MD) · m.m.brands@amsterdamumc.nl
    Contact: Principal Investigator (Marion Brands, MD)

  • Comenius University in Bratislva, Bratislava, Slovakia

  • University Hospital Bern Inselspital, Bern, Switzerland

  • Great Ormond Street Hospital, London, United Kingdom

  • Royal Free London NHS Foundation Trust, London, United Kingdom

  • Royal Manchester Children's Hospital, Manchester, United Kingdom

View source on ClinicalTrials.gov(opens in a new tab)