Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)
Abroad (travel likely)CompletedPHASE2
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Conditions
Bone Marrow Failure Syndrome · Congenital Amegakaryocytic Thrombocytopenia · Diamond-Blackfan Anemia · Hereditary Sideroblastic Anemia · Paroxysmal Nocturnal Hemoglobinuria · Shwachman-Diamond Syndrome · Hematologic Neoplasm With Germline GATA2 Mutation · Hematologic Neoplasm With Germline SAMD9 Mutation · Hematologic Neoplasm With Germline SAMD9L Mutation
Locations
- Children's Hospital Los Angeles, Los Angeles, California, United States
- Rady Children's Hospital/UCSD, San Diego, California, United States
- University of California San Francisco, San Francisco, California, United States
- Children's Hospital Colorado, Aurora, Colorado, United States
- Children's Healthcare of Atlanta, Atlanta, Georgia, United States
- Johns Hopkins University, Baltimore, Maryland, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- University of Michigan Medical Center, Ann Arbor, Michigan, United States
- University of Minnesota, Minneapolis, Minnesota, United States
- St. Louis Children's Hospital, St Louis, Missouri, United States
- Roswell Park Comprehensive Cancer Center, Buffalo, New York, United States
- Memorial Sloan Kettering Cancer Center, New York, New York, United States
- Cohen Children's Hospital of NY, Queens, New York, United States
- Duke University Medical Center, Durham, North Carolina, United States
- Cincinnati Children's Hospital, Cincinnati, Ohio, United States
- Nationwide Children's Hospital, Columbus, Ohio, United States
- Oregon Health & Science University, Portland, Oregon, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- Vanderbilt University Medical Center, Nashville, Tennessee, United States
- MD Anderson Cancer Center, Houston, Texas, United States
- Texas Children's Hospital, Houston, Texas, United States
- Primary Children's/University of Utah, Salt Lake City, Utah, United States
- Fred Hutch/University of Washington Cancer Consortium, Seattle, Washington, United States
- Medical College of Wisconsin/Children's Hospital of Wisconsin, Milwaukee, Wisconsin, United States