Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of Bone Marrow Failure Diseases (BMT CTN 1904)
Conditions
Bone Marrow Failure Syndrome · Congenital Amegakaryocytic Thrombocytopenia · Diamond-Blackfan Anemia · Hereditary Sideroblastic Anemia · Paroxysmal Nocturnal Hemoglobinuria · Shwachman-Diamond Syndrome · Hematologic Neoplasm With Germline GATA2 Mutation · Hematologic Neoplasm With Germline SAMD9 Mutation · Hematologic Neoplasm With Germline SAMD9L Mutation
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Children's Hospital Los Angeles, Los Angeles, California, United States
Rady Children's Hospital/UCSD, San Diego, California, United States
University of California San Francisco, San Francisco, California, United States
Children's Hospital Colorado, Aurora, Colorado, United States
Children's Healthcare of Atlanta, Atlanta, Georgia, United States
Johns Hopkins University, Baltimore, Maryland, United States
Boston Children's Hospital, Boston, Massachusetts, United States
University of Michigan Medical Center, Ann Arbor, Michigan, United States
University of Minnesota, Minneapolis, Minnesota, United States
St. Louis Children's Hospital, St Louis, Missouri, United States
Roswell Park Comprehensive Cancer Center, Buffalo, New York, United States
Memorial Sloan Kettering Cancer Center, New York, New York, United States
Cohen Children's Hospital of NY, Queens, New York, United States
Duke University Medical Center, Durham, North Carolina, United States
Cincinnati Children's Hospital, Cincinnati, Ohio, United States
Nationwide Children's Hospital, Columbus, Ohio, United States
Oregon Health & Science University, Portland, Oregon, United States
Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Vanderbilt University Medical Center, Nashville, Tennessee, United States
MD Anderson Cancer Center, Houston, Texas, United States
Texas Children's Hospital, Houston, Texas, United States
Primary Children's/University of Utah, Salt Lake City, Utah, United States
Fred Hutch/University of Washington Cancer Consortium, Seattle, Washington, United States
Medical College of Wisconsin/Children's Hospital of Wisconsin, Milwaukee, Wisconsin, United States
Study leads
Lauri Burroughs, MD
Study Chair
Fred Hutch/University of Washington Cancer Consortium
Margaret MacMillan, MD
Study Chair
University of Minnesota