Direct Lentiviral Injection Gene Therapy for MLD

Abroad (travel likely)Recruiting

Conditions

Metachromatic Leukodystrophy (MLD)

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
Study leads
  • Lung-Ji Chang, Ph.D

    Principal Investigator

    Shenzhen Geno-Immune Medical Institute