Direct Lentiviral Injection Gene Therapy for MLD
Conditions
Metachromatic Leukodystrophy (MLD)
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Lung-Ji Chang, Shenzhen, Guangdong, China
Study leads
Lung-Ji Chang, Ph.D
Principal Investigator
Shenzhen Geno-Immune Medical Institute