Phase III Study of Edasalonexent in Boys With Duchenne Muscular Dystrophy
Conditions
Muscular Dystrophy, Duchenne
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Arkansas Children's Hospital, Little Rock, Arkansas, United States
Children's Hospital of Los Angeles, Los Angeles, California, United States
UC Davis, Sacramento, California, United States
Nemours Children's Hospital, Orlando, Florida, United States
Rare Disease Research, LLC, Atlanta, Georgia, United States
Rush University Children's Hospital, Chicago, Illinois, United States
University of Iowa Children's Hospital, Iowa City, Iowa, United States
University of Kansas Medical Center, Fairway, Kansas, United States
Kennedy Krieger Institute, Baltimore, Maryland, United States
Johns Hopkins School of Medicine, Baltimore, Maryland, United States
Boston Children's Hospital, Boston, Massachusetts, United States
University of Michigan, Ann Arbor, Michigan, United States
University of Minnesota, Minneapolis, Minnesota, United States
Las Vegas Clinic, Las Vegas, Nevada, United States
Cincinnati Children's Hospital, Cincinnati, Ohio, United States
MetroHealth Medical Center, Cleveland, Ohio, United States
Shriners Hospitals for Children, Portland, Oregon, United States
Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Vanderbilt University Medical Center, Nashville, Tennessee, United States
Cook Children's Medical Center, Fort Worth, Texas, United States
University of Texas Health Science Center at San Antonio, San Antonio, Texas, United States
University of Utah, Salt Lake City, Utah, United States
Children's Hospital of the King's Daughters, Norfolk, Virginia, United States
Children's Hospital of Richmond at VCU, Richmond, Virginia, United States
The Children's Hospital at Westmead, Westmead, New South Wales, Australia
Children's Health Queensland Children's Hospital and Health Service, South Brisbane, Queensland, Australia
Royal Children's Hospital, Parkville, Victoria, Australia
Alberta Children's Hospital, Calgary, Alberta, Canada
London Health Sciences Centre - Children's Hospital, London, Ontario, Canada
Children's Hospital of Eastern Ontario, Ottawa, Ontario, Canada
CHU Sainte-Justine, Montreal, Quebec, Canada
University of Hamburg, Hamburg, Germany
University of Munich, Munich, Germany
Children's University Hospital, Dublin, Ireland
Hadassah Medical Center, Jerusalem, Israel
Queen Silvia Children's Hospital, Gothenburg, Sweden
Bristol Children's Hospital, Bristol, United Kingdom
Evelina Children's Hospital, London, United Kingdom
Great Ormond Street Hospital (GOSH), London, United Kingdom
Royal Manchester Children's Hospital, Manchester, United Kingdom
Study leads
Joanne M Donovan, Chief Medical Officer, MD, PhD
Study Chair
Catabasis Pharmaceuticals