Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study

IsraelRecruitingPHASE2, PHASE3

Conditions

Duchenne Muscular Dystrophy

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • University of California - Davis Medical Center - Devis Physical Medicine & Rehabilitation, Sacramento, California, United States

  • Rady Children's Hospital center - UCSD Department of Neuroscience, San Diego, California, United States

  • Connecticut Children's Medical Center, Neurology Division, Hartford, Connecticut, United States

  • Child Health Research Institute, Gainesville, Florida, United States

  • MD Rare Disease Research, LLC, Atlanta, Georgia, United States

  • University of Iowa Children's Hospital, Iowa City, Iowa, United States

  • Washington University School of Medicine in St Louis Department of Neurology 660 S.Euclid Avenue, Campus Box 8111, St Louis, Missouri, United States

  • Shriners Hospitals for Children, Portland, Oregon, United States

  • The Children's Hospital of Philadelphia Colket Translational Research Building, Philadelphia, Pennsylvania, United States

  • Virginia Commonwealth University Childrens Hospital of Richmond at, Richmond, Virginia, United States

  • University Hospitals Leuven, Neuromuscular Reference Centre, Child Neurology, Leuven, Belgium

  • Hospital de La Citadelle, Centre de Référence des Maladies Neuromuscolaires (CRMN), Liège, Belgium

  • Kinsmen Research Centre - Alberta Children's Hospital, Calgary, Alberta, Canada

  • The University of British Columbia, Children's and Womens Health Centre of BC Branch, Vancouver, British Columbia, Canada

  • Holland Bloorview Kids Rehabilitation Hospital, Toronto, Ontario, Canada

  • CHU de Nantes - Hotel-Dieu - Hopital Nord Laennec, rez-de-chausse haut ail Ouest, Nantes, France

  • Hôpital Armand Trousseau I-Motion - Plateforme d'essais cliniques pédiatriques Bâtiment Lemariey - Porte 20 * 2ème étage 26 Avenue du Dr Arnold Nette, Paris, France

  • Universitätsklinikum Essen - Kinder-und Jugendmedizin Neuropadiatrie, Essen, Germany

  • Klinik- und Poliklinik fur Kinder- und Jugendmedizin, Universitatsklinikum HamburgEppendorf, Martinistr. 52, Hamburg, Germany

  • Klinikum der Universitat Munchen, Campus Innenstadt, Lindwurmstr. 4, München, Germany

  • Institute of Neurology - Schneider Children's Medical Center of Israel Kaplan, 14, Petah Tikva, Israel

  • U.O.S.D. Centro Traslazionale di Miologia e Patologie Neurodegenerative, Building 16 - ground floor IRCCS Istituto Giannina Gaslini,, Genova, Italy

    Contact: Study coordinator (Claudio Bruno, MD) · claudio2246@gmail.com · +39 010 56362 2620
    Contact: Principal Investigator (Claudio Bruno, MD)
  • A.O.U. Policlinico G. Martino, U.O.C. Neurologia e Malattie Neuromuscolari, Messina, Italy

  • Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano, UOS di Neurologia Pediatrica, Milan, Italy

  • IRCCS Istituto Neurologico Carlo Besta, Milan, Italy

  • Centro Clinico NeMO Fondazione Serena ONLUS Area SUD, Milan, Italy

  • Ospedale Pediatrico Bambino Gesù, Malattie Neuromuscolari e Neurodegenerative, Roma, Italy

    Contact: Study coordinator (Enrico Bertini, MD) · enricosilvio.bertini@opbg.net
    Contact: Principal Investigator (Enrico Bertini, MD)
  • Fondazione Policlinico Universitario "A.Gemelli", UOC Neuropsichiatria Infantile, Roma, Italy

  • Leiden University Medical Center LUMC, Albinusdreef 2, Leiden, Netherlands

  • Radboud University Medical Centre, Nijmegen, Netherlands

  • Clinic of Neurology and Psychiatry for Children and Youth - Neurology Department Dr. Subotic 6a,, Belgrade, Serbia

  • Neuromuscular Pathology Unit - Hospital Sant Joan de Déu, Esplugues de Llobregat, Barcellona, Spain

  • Hospital Materno-Infantil, Barcelona, Spain

    Contact: Study coordinator (Francina Munell, MD) · francina.munell@vhir.org
    Contact: Principal Investigator (Francina Munell, MD)
  • Hospital Universitario Virgen del Rocio, Seville, Spain

  • Hospital Universitari i Politècnic La Fe - Servicio Neurologia, Valencia, Spain

  • Alder Hey Children's Hospital NHS Trust, Liverpool, UK, United Kingdom

  • The Robert Jones and Agnes Hunt Orthopaedic Hospital NHS Foundation Trust, Gobowen, United Kingdom

  • UCL Great Ormond Street Institute of Child Health, Dubowitz Neuromuscular Centre and MRC Centre for NMD, London, United Kingdom

  • The John Walton Muscular Dystrophy Research Centre, Newcastle upon Tyne, United Kingdom