A Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia

Abroad (travel likely)CompletedPHASE3

Conditions

Achondroplasia

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Children's Hospital & Research Center Oakland, Oakland, California, United States

  • Harbor - UCLA Medical Center, Torrance, California, United States

  • Alfred I. duPont Hospital for Children, Wilmington, Delaware, United States

  • Emory University, Decatur, Georgia, United States

  • Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States

  • Johns Hopkins University, Baltimore, Maryland, United States

  • University of Missouri, Columbia, Missouri, United States

  • Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States

  • Baylor College of Medicine, Houston, Texas, United States

  • Seattle Children's Hospital, Seattle, Washington, United States

  • Medical College of Wisconsin, Children's Hospital, Milwaukee, Wisconsin, United States

  • The Children's Hospital at Westmead, Westmead, New South Wales, Australia

  • Murdoch Children's Research Institute, Parkville, Victoria, Australia

  • Otto-von-Guericke Universitaet, Universitaetskinderklinik, Magdeburg, Germany

  • Universitätsklinikum Münster, Münster, Germany

  • Osaka University Hospital, Osaka, Japan

  • Saitama Children's Medical Center, Saitama, Japan

  • Tokushima University Hospital, Tokushima, Japan

  • Institut Catala de Traumatologica I Medicina de l'Esport, Barcelona, Spain

  • Hospital Sant Joan de Deu, Barcelona, Spain

  • Hospital Universitario Virgen de la Victoria, Málaga, Spain

  • Acibadem University School of Medicine, Istanbul, Turkey (Türkiye)

  • Guy's and St. Thomas NHS Foundation Trust Evelina Children's Hospital, London, United Kingdom

  • Sheffield Children's NHS Foundation Trust, Sheffield, United Kingdom

Study leads
  • Medical Director, MD

    Study Director

    BioMarin Pharmaceutical