A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients

חו"ל (דורש נסיעה)מגייס משתתפיםPHASE1

מצבים רפואיים

AADC Deficiency

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים

University of California San Francisco, Benioff Children's Hospital, San Francisco, California, United States
Contact: Study coordinator (Catalina Pen) · catalina.pen@ucsf.edu
E
Contact: Principal Investigator (Nalin Gupta, MD)
Nationwide Children's Hospital, Columbus, Ohio, United States
Contact: Study coordinator (Hannah Lehmann) · hannah.lehmann@nationwidechildrens.org
Contact: Study coordinator (Margaret Carey) · margaret.carey@nationwidechildrens.org
Contact: Principal Investigator (Jeffrey Leonard, MD)
Toni Pearson, MD (Sub-investigator)
The Ohio State University Medical Center, Columbus, Ohio, United States
Contact: Study coordinator (Andrea Davis, MS) · andrea.davis@osumc.edu · 614-814-6871
Contact: Principal Investigator (Russell Lonser, MD)
Krystof Bankiewicz, PhD (Sub-investigator)

מובילי המחקר

Krystof Bankiewicz, MD, PhD
Study Director
OSU Professor of Neurological Surgery