UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Abroad (travel likely)RecruitingPHASE1

Conditions

Adrenoleukodystrophy · Batten Disease · Mucopolysaccharidosis II · Leukodystrophy, Globoid Cell · Leukodystrophy, Metachromatic · Neimann Pick Disease · Pelizaeus-Merzbacher Disease · Sandhoff Disease · Tay-Sachs Disease · Brain Diseases, Metabolic, Inborn · Alpha-Mannosidosis · Sanfilippo Mucopolysaccharidoses

Simple summaryAI-assisted

This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.

Locations
  • Duke University Medical Center, Durham, North Carolina, United States

    Contact: Study coordinator (Sydney Crane, RN) · cordbloodtherapyinfo@dm.duke.edu
    Contact: Principal Investigator (Joanne Kurtzberg, MD)
    Jessica Sun, MD (Sub-investigator)
Study leads
  • Joanne Kurtzberg, MD

    Principal Investigator

    Duke University