UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Conditions
Adrenoleukodystrophy · Batten Disease · Mucopolysaccharidosis II · Leukodystrophy, Globoid Cell · Leukodystrophy, Metachromatic · Neimann Pick Disease · Pelizaeus-Merzbacher Disease · Sandhoff Disease · Tay-Sachs Disease · Brain Diseases, Metabolic, Inborn · Alpha-Mannosidosis · Sanfilippo Mucopolysaccharidoses
Simple summaryAI-assisted
This summary is produced by a language model and is experimental. It may be incomplete or inaccurate and is not a substitute for professional medical advice.
Locations
Duke University Medical Center, Durham, North Carolina, United States
Contact: Principal Investigator (Joanne Kurtzberg, MD)Jessica Sun, MD (Sub-investigator)
Study leads
Joanne Kurtzberg, MD
Principal Investigator
Duke University