Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canada

ישראלהושלםPHASE3

מצבים רפואיים

Duchenne Muscular Dystrophy · Becker Muscular Dystrophy · Dystrophinopathy

סיכום בשפה פשוטהבעזרת בינה מלאכותית

הסיכום נכתב על־ידי מודל שפה והוא ניסיוני. המידע עלול להיות חלקי או שגוי ואינו תחליף לייעוץ רפואי.

מיקומים
  • Royal Children's Hospital, Parkville, Melbourne, Australia

  • Institute For Neuromuscular Research, The Children's Hospital at Westmead, Westmead, Australia

  • University Hospital KU Leuven, Leuven, Belgium

  • Alberta Children's Hospital, Calgary, Alberta, Canada

  • British Columbia Children's Hospital, Vancouver, British Columbia, Canada

  • Children's Hospital of Western Ontario, London, Ontario, Canada

  • Hôpital d'Enfants CHU Timone, Marseille, France

  • Laboratoire d'Exploration Fonctionnelles, Nantes, France

  • Groupe Hospitalier La Pitie-Salpetriere, Paris, France

  • University of Essen - Clinic for Children, Essen, Germany

  • University Hospital, Freiburg im Breisgau, Germany

  • Hadassah Medical Center, Hebrew University Hospital, Jerusalem, Israel

  • Ospedale Maggiore Policlinico in Milan, Milan, Italy

  • Ospedale Pediatrico Bambino Gesu, Rome, Italy

  • U.O. Complessa di Neuropsichiatria Infantile, Rome, Italy

  • Hospital Sant Joan de déu, Barcelona, Spain

  • Hospital Universitari La Fe, Valencia, Spain

  • Queen Silvia Children's Hospital, Gothenburg, Sweden

  • Astrid Lindgren Pediatric Hospital, Stockholm, Sweden

  • Great Ormond Street Hospital, London, United Kingdom

  • University of Newcastle Institute of Human Genetics, Newcastle upon Tyne, United Kingdom

מובילי המחקר
  • Edward O'Mara, MD

    Study Director

    PTC Therapeutics