Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canada
IsraelCompletedPHASE3
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Conditions
Duchenne Muscular Dystrophy · Becker Muscular Dystrophy · Dystrophinopathy
Locations
- Royal Children's Hospital, Parkville, Melbourne, Australia
- Institute For Neuromuscular Research, The Children's Hospital at Westmead, Westmead, Australia
- University Hospital KU Leuven, Leuven, Belgium
- Alberta Children's Hospital, Calgary, Alberta, Canada
- British Columbia Children's Hospital, Vancouver, British Columbia, Canada
- Children's Hospital of Western Ontario, London, Ontario, Canada
- Hôpital d'Enfants CHU Timone, Marseille, France
- Laboratoire d'Exploration Fonctionnelles, Nantes, France
- Groupe Hospitalier La Pitie-Salpetriere, Paris, France
- University of Essen - Clinic for Children, Essen, Germany
- University Hospital, Freiburg im Breisgau, Germany
- Hadassah Medical Center, Hebrew University Hospital, Jerusalem, Israel
- Ospedale Maggiore Policlinico in Milan, Milan, Italy
- Ospedale Pediatrico Bambino Gesu, Rome, Italy
- U.O. Complessa di Neuropsichiatria Infantile, Rome, Italy
- Hospital Sant Joan de déu, Barcelona, Spain
- Hospital Universitari La Fe, Valencia, Spain
- Queen Silvia Children's Hospital, Gothenburg, Sweden
- Astrid Lindgren Pediatric Hospital, Stockholm, Sweden
- Great Ormond Street Hospital, London, United Kingdom
- University of Newcastle Institute of Human Genetics, Newcastle upon Tyne, United Kingdom